300 million people in the world live with a rare disease, united by common challenges, many resulting from poor visibility and knowledge of their disease. Orphanet’s powerful knowledge base, accessible through a range of ressources including those presented here on www.orphadata.com, provides the data needed to improve every step of the care pathway.​​

The Orphanet knowledge base is structured around the Orphanet nomenclature of rare diseases, a dedicated and globally-recognised standard that improves data interoperability between healthcare and research information systems. The Orphanet knowledge base is developed, maintained and coordinated by the US14-Orphanet department at the French National Institute of Health and Medical Research in Paris, France. Orphanet also produces the Orphadata platform.​

The Orphadata platform provides access to a range of resources, services and tools derived from the Orphanet knowledge base. One of these resources is Orphadata Science, comprised of comprehensive, high-quality downloadable datasets and ontologies derived from the Orphanet knowledge base, made available through the CC BY 4.0 licence in a reusable and computable format. Orphadata Science has been designated as an ELIXIR Core Data Resource and a Global Core Biodata Resource, thus recognising their contribution to the biodata ecosystem. Orphadata Science resources and licencing information are clearly indicated on this site. ​​

The Orphadata platform also provides access to resources aimed at faciliating the integration of the Orphanet nomenclature of rare diseases –  ORPHAcodes into information systems, and to an expanding range of request datasets, services and tools,  Orphadata Products, where the access may vary depending on your status and intended use. ​